Category Archives: Congenital disorders

Born with a heart malformation: The children forgotten by the Mexican health system

When Nevith was five years old, her heart began to hurt. She used to tell her mother that “it beat fast, as if it was going to jump out of her little chest. When she walked fast her heartbeat quickened, but sometimes it also happened when she was asleep, and she woke up scared,” says […]

The Role of a Multidisciplinary Approach, Guidelines for Management in Patients with RSV

[embedded content] In this multidisciplinary roundtable discussion, Albert Rizzo, MD, interviews Barbara Taylor, MD, MS, and Leonard R. Krilov, MD, about guidelines in the management of patients with RSV, including pediatrics VS adults and how to differentiate RSV, influenza, and COVID-19. For more respiratory syncytial virus content, visit the disease state hub.  TRANSCRIPTION: Albert A. Rizzo, […]

Phoenix Children’s Hires World-Renowned Scientists, Improves Understanding of Childhood Illnesses

PHOENIX, Ariz., Oct. 26, 2023 /PRNewswire/ — Phoenix Children’s is taking another leap forward with the addition of two internationally recognized scientists and new research efforts that will improve quality and outcomes for children facing a range of illnesses. “We are thrilled to welcome two brilliant researchers whose knowledge and expertise expand our purview and add […]

Rivogenlecleucel by Bellicum Pharmaceuticals for Osteopetrosis: Likelihood of Approval

GlobalData tracks drug-specific phase transition and likelihood of approval scores, in addition to indication benchmarks based off 18 years of historical drug development data. Attributes of the drug, company and its clinical trials play a fundamental role in drug-specific PTSR and likelihood of approval. Rivogenlecleucel overview Rivogenlecleucel (BPX-501) is under development for the treatment of […]

Rivogenlecleucel by Bellicum Pharmaceuticals for Aplastic Anemia: Likelihood of Approval

GlobalData tracks drug-specific phase transition and likelihood of approval scores, in addition to indication benchmarks based off 18 years of historical drug development data. Attributes of the drug, company and its clinical trials play a fundamental role in drug-specific PTSR and likelihood of approval. Rivogenlecleucel overview Rivogenlecleucel (BPX-501) is under development for the treatment of […]

Trehalose by Seelos Therapeutics for Oculopharyngeal Muscular Dystrophy: Likelihood of Approval

GlobalData tracks drug-specific phase transition and likelihood of approval scores, in addition to indication benchmarks based off 18 years of historical drug development data. Attributes of the drug, company and its clinical trials play a fundamental role in drug-specific PTSR and likelihood of approval. Trehalose overview Trehalose is under development for the treatment of oculopharyngeal […]

Deaths due to homicide are the second-highest cause of injury-related mortality in children aged one to 14, audit finds

Deaths due to homicide or filicide accounted for 17.8pc of all injury-related deaths during 2019 and 2021, compared with 6.6pc between 2007 and 2018. The vast majority of these deaths ­occurred in the child’s own home and were committed by a family member or someone known to the child. The National Paediatric Mortality Register (NPMR) […]